[논문] Advances in Therapeutic Applications of CRISPR Genome Editing for Spinal Pain Management
[논문] Functional assessment of all ATM SNVs using prime editing and deep learning
[논문] A rational engineering strategy for structural dynamics modulation enables target specificity enhancement of the Cas9 nuclease
[논문] Programmable RNA acetylation with CRISPR-Cas13
[논문] Evaluating the Therapeutic Potential of Superoxide Dismutase in a Rat Model of Wet Age-Related Macular Degeneration
[논문] Intravitreal adenine base editing of RS1 improves vision in a preclinical mouse model of retinoschisis
[논문] Autophagy induction enhances homologous recombination-associated CRISPR-Cas9 gene editing
[논문] An innovative approach using CRISPR-ribonucleoprotein packaged in virus-like particles to generate genetically engineered mouse models
[논문] Systematic genetic assessment of hearing loss using whole-genome sequencing identifies pathogenic variants
[논문] Clinical Characterization, Natural History, and Detailed Phenotyping of NMNAT1-Associated Leber Congenital Amaurosis
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